Biomarkers for prediction of skeletal disease progression in mucopolysaccharidosis type I.
Lund TC, Doherty TM, Eisengart JB, Freese RL, Rudser KD, Fung EB, Miller BS, White KK, Orchard PJ, Whitley CB, Polgreen LE.
Lund TC, et al.
JIMD Rep. 2020 Dec 8;58(1):89-99. doi: 10.1002/jmd2.12190. eCollection 2021 Mar.
JIMD Rep. 2020.
PMID: 33728251
Free PMC article.
Linear regression tested for associations of change in biomarkers over the first year with change in long-term outcomes. RESULTS: MPS I participants (N = 19) were age 5 to 16 years and on average 6.9 2.9 years post treatment initiation. ...
Linear regression tested for associations of change in biomarkers over the first year with change in long-term outcomes. RESULTS: MPS …